France has positioned itself as a leader in rare disease research, patient care, and data management through the development of the French National Database of Rare Diseases (BNDMR). This comprehensive and secure national health data repository is a fundamental component of France’s national rare disease plans (PNMR), with over 750,000 registered patients across more than […]

At BlueDil International, we are entering a new chapter—one that reflects our commitment to innovation, strategic growth and leadership excellence. We are proud to announce a transition in our executive team as Sylvain Forget, our founder and long-standing leader, passes the baton to Leonardo Calzetti, who will be the new CEO. Since the birth of […]

The Role of PAGs in European Decision-Making Processes  In several European countries, patient organizations are playing an increasingly crucial role in Health Technology Assessment (HTA) and regulatory decision-making:  – European Union: The new HTA Regulation, set to take effect in 2025, encourages patient associations to participate in Joint Scientific Consultations and Joint Clinical Assessments, fostering […]

Sylvain Forget Co-Founder & Senior Partner, France 1. What inspired your dedication to the rare disease landscape? My dedication to the rare disease landscape stems from a deep conviction that every patient, regardless of the rarity of their condition, deserves access to appropriate care, treatment, and support. After many years working in non-orphan pharma sector, […]